Paper page

Original: publisher page

Niraj S. Trasi, Lynne S. Taylor* · Journal of Pharmaceutical Sciences 104, 2583-2593 (2015)

Thermodynamics of Highly Supersaturated Aqueous Solutions of Poorly Water-Soluble Drugs—Impact of a Second Drug on the Solution Phase Behavior and Implications for Combination Products

When two poorly soluble drugs are both highly supersaturated in water they share one drug-rich phase, so the highest free concentration each can reach (its "amorphous solubility") drops, roughly in proportion to its mole fraction in that phase, and membrane flux drops with it.

Abbreviations

LLPS liquid–liquid phase separation; RTV ritonavir; LPV lopinavir; PTX paclitaxel; HPMC hydroxypropyl methylcellulose; Sa, Sc amorphous and crystalline solubility; Sa° amorphous solubility of the pure drug; x1 mole fraction of drug 1 in the drug-rich phase; I3/I1 ratio of the pyrene emission peaks at 383 and 373 nm; DLS dynamic light scattering.

Story. Why they did it → how → what they found → how it fits together → what is left. Each part opens with the short version; "More detail" under it gives the full account. Grey ids open the evidence behind a sentence.

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Question

Does a second drug change the concentration at which a supersaturated drug separates into a drug-rich phase, and so the free concentration and membrane flux each drug can reach?

Short answer

Yes, when the second drug is unionized and mixes with the first. With 10 µM lopinavir, paclitaxel or felodipine present, ritonavir separated at about 14, 10 and 12 µg/mL instead of about 26 µg/mL; in 30 + 30 µg/mL mixtures the free concentration of each drug fell to 8–15 µg/mL, and its flux fell with it. Ionized diclofenac did not mix into a ritonavir-rich phase. ···

Conclusion

For ritonavir combined with lopinavir, paclitaxel or felodipine in pH 6.8 buffer, a second unionized drug lowers the concentration at which a drug-rich phase forms and the free concentration each drug can reach; the authors read this as the two drugs mixing in one drug-rich phase, which lowers each drug's "amorphous solubility" ("suggests"). ··· Lopinavir added to an existing ritonavir-rich phase partitions largely into it, and the ritonavir–lopinavir bulk concentrations follow an ideal-mixing model ("good agreement", "nearly ideally"); the model was tested on this one pair. ·· Membrane flux of both drugs falls in the mixtures, and free concentrations estimated from flux and from ultracentrifugation agree within experimental error. · Ionized diclofenac does not mix, which the authors explain by its charge. · The authors' extensions to co-amorphous products, co-dosing, in vitro metabolic assays and bioavailability ("would be expected", "potential implications") were not tested. ···

01Why this study

Known 1Above its amorphous solubility, a drug forms a drug-rich phase

A highly supersaturated drug separates by LLPS into colloidal drug-rich droplets once it passes its "amorphous solubility", typically 5–50 times the crystalline solubility.

Ilevbare 2013, ref 7; Almeida e Sousa 2015, ref 8 ·

Known 2That point caps free drug and flux

Beyond it, added drug only makes more drug-rich phase; the free concentration and the membrane flux stay at their maximum.

Raina 2014, ref 13

Known 3Other molecules can enter the drug-rich phase

Fluorescence probes mix into it.

Ilevbare 2013, ref 7

Known 4Drugs often meet in solution

Kaletra puts ritonavir and lopinavir in one ASD, and ritonavir is co-dosed to boost other drugs.

Zeldin 2004, ref 15 ·

Gap → this paperWhat does a second drug do to the free concentration a supersaturated drug can reach?
More detail

What was already known. The introduction builds on these points:

  • Drug aggregates matter in screening. Diluting a DMSO or other organic stock into an aqueous assay can give a non-crystalline drug-rich colloidal phase ("promiscuous aggregation"), held responsible for many false results in enzymatic high-throughput screens and reported to reduce the cytotoxicity of anticancer drugs. (Coan 2008, ref 2; Owen 2012, ref 3)
  • The same colloids may help oral delivery. Anti-HIV compounds forming aggregates of 100 nm or less showed higher than expected oral bioavailability, and amorphous dosage forms release colloidal species that could improve bioavailability ("it has been suggested"). (Frenkel 2005, ref 4; Friesen 2008, ref 5)
  • The colloids are a drug-rich liquid phase. Above the amorphous solubility (typically 5–50 times the crystal solubility) the drug's liquid miscibility limit is exceeded and LLPS gives a drug-rich phase of initially colloidal size; it is a water-saturated supercooled liquid or a glass, and it may later crystallize; some drugs crystallize directly. The authors adopt "drug-rich phase" instead of "drug aggregates". (refs 2, 6–11) ·
  • The amorphous solubility can be predicted. It can be estimated from the crystal solubility and the crystal–supercooled liquid free energy difference, with excellent agreement; LLPS has been produced by dilution from organic solvent, pH shift, ASD dissolution and temperature change. (Almeida e Sousa 2015, ref 8; refs 6, 7, 12)
  • Free drug and flux peak at LLPS. Once the drug-rich phase forms, the bulk free drug concentration is at its maximum (the chemical potential is constant in an equilibrated two-phase system), and transport across a semipermeable membrane peaks at the concentration where the drug-rich phase first forms. (Raina 2014, ref 13)
  • The drug-rich phase interacts with other species. Enzymes may adsorb to it and be inactivated, and environment-sensitive probes mix preferentially into it. (Coan 2009, ref 14; Ilevbare 2013, ref 7)
  • Two drugs in solution together is common. Combination products such as Kaletra (ritonavir and lopinavir as an ASD), separate products dosed at the same time, and metabolic assays that combine a substrate with a test compound all put two drugs into solution together. Ritonavir is often co-dosed because it inhibits CYP3A4 and so boosts the bioavailability of a second drug, and it readily forms a drug-rich phase. (Zeldin 2004, ref 15; Ilevbare 2013, ref 7) ·

What the paper set out to do. Find out how drug-rich phases form in solutions with more than one solute and how a second solute changes the free concentration of each drug. The hypothesis was that a compound's free drug concentration falls when a second compound that readily undergoes LLPS is present.

02How they approached it

Ritonavir, which readily forms a drug-rich phase and is often co-dosed, was the anchor drug. First each drug's own amorphous solubility was pinned down by four methods; then a second drug was added and the onset of phase separation, the bulk (free) concentrations, partitioning into an existing drug-rich phase and membrane flux were measured, and the bulk data were compared with an ideal-mixing model. All media were 100 mM phosphate buffer, pH 6.8. ··

RitonavirRTV, HIV protease inhibitorThe anchor drug in every pair; amorphous solubility 26–28 µg/mL; measured. ·
LopinavirLPV, HIV protease inhibitorUnionized partner, structurally similar to ritonavir; amorphous solubility 16–17.3 µg/mL; measured by every method and modelled. ··
PaclitaxelPTX, taxane; supplied as a hydrateUnionized partner; amorphous solubility 27.2–30.1 µg/mL; measured by fluorescence onset and flux. ···
FelodipinedihydropyridineUnionized partner that separates at about 5–6 µg/mL (literature values); measured by fluorescence onset only. ··
Diclofenacweak acid, pKa 4.2Ionized at pH 6.8; tested only for mixing into a ritonavir drug-rich phase. ·

What was done

Experiment

Each drug alone in buffer→crystal solubility and LLPS concentration by UV extinction, pyrene fluorescence and ultracentrifugation.····

Experiment

Diffusion cell→flux versus donor concentration→break point.·

↓
Experiment

Second solute at a fixed molar concentration, ritonavir added stepwise→onset of LLPS by pyrene I3/I1 or felodipine emission.··

Experiment

Lopinavir added to 5–30 µg/mL ritonavir→ultracentrifugation→both drugs in the supernatant.·

↓
Experiment

Lopinavir or diclofenac added to a pre-formed ritonavir drug-rich phase→bulk concentrations.···

Experiment

30 + 30 µg/mL binary donors→flux of each drug→free concentration from flux and from ultracentrifugation.··

↓
Model

Ideal mixing in the drug-rich phase with single-drug amorphous solubility→predicted bulk concentrations.·

Comparison

Predicted versus measured bulk ritonavir and lopinavir against drug-rich phase mole fraction.

More detail

What was done

  1. Single drugs. Crystal solubility: excess crystals in 15 mL buffer, shaken 2 days at 25 °C, ultracentrifuged, HPLC. LLPS concentration three ways: (1) a methanolic stock added to buffer with 10 µg/mL HPMC, ultracentrifuged at 274,355×g, supernatant by HPLC; (2) pyrene added as a polarity probe, whose I3/I1 ratio rises from about 0.51 to about 0.61 when a drug-rich phase forms; (3) continuous addition of drug by syringe pump at 25 °C with UV extinction at 350 nm. HPMC was needed for paclitaxel, which otherwise crystallized; ritonavir and lopinavir gave the same value without it. ·····
  2. Flux. A side-by-side diffusion cell (30 mL each side, regenerated cellulose membrane of 6–8 kDa cut-off, 30 mm diameter, 25 °C, buffer with 10 µg/mL HPMC); flux is the slope of receiver concentration versus time. Single drugs over 4–60 µg/mL; binary donors of 30 µg/mL each of ritonavir with paclitaxel or with lopinavir. ·
  3. Onset with a second drug. Lopinavir, paclitaxel or felodipine at 10 µM (and 5–20 µM) in pyrene solution, ritonavir added stepwise; the onset is where I3/I1 (or, for autofluorescent felodipine, its 430 nm emission) starts to rise. The methods give 4 µg/mL for these solutions, the results 10 µM. ·
  4. Binary ultracentrifugation. Lopinavir (5–30 µg/mL) added to 5, 10, 15 and 30 µg/mL ritonavir; both drugs measured in the supernatant; some pellets dissolved to check mass balance. ·
  5. Existing drug-rich phase. Ritonavir at 45 µg/mL (well above its own limit) to form a drug-rich phase, then lopinavir (4–16 µg/mL) or diclofenac (4–20 µg/mL; measured by UV at 275 and 252 nm) added; ritonavir also raised to 65 and 85 µg/mL with 16 µg/mL lopinavir. ·
  6. Free concentration in mixtures. Flux of each drug in the binary donor converted to a free concentration with the single-drug flux curves, and checked by ultracentrifuging solutions of the donor composition. ·
  7. Model. Ritonavir mole fraction in the drug-rich phase from mass balance (added minus supernatant); predicted bulk concentrations from Eq. 4 with the single-drug amorphous solubilities, under four stated assumptions. ·

Key equations

Amorphous versus crystal solubility (Eq. 1)
μ1∘−μ1c∘RT=lnSaSc

The amorphous drug, treated as a supercooled liquid, has a higher chemical potential than the crystal, so its solubility Sa is higher than the crystal solubility Sc by the factor exp(Δμ/RT).·

Ideal mixing in the drug-rich phase (Eqs. 2, 3)
μ1=μ1∘+RTlnx1μ2=μ2∘+RTln(1−x1)

If the two amorphous drugs mix ideally, each drug's chemical potential in the shared phase is lowered by RT ln of its mole fraction.··

Amorphous solubility of a mixture (Eq. 4)
Sa(x1)=Sa∘x1

The free concentration in equilibrium with the mixed drug-rich phase is the pure drug's amorphous solubility times its mole fraction in that phase; the same form with (1 − x1) gives the partner. The paper uses it with the single-drug values of Table 1 and no fitted parameter.·

Terms used on this page
  • Amorphous solubility (Sa): the concentration at which a supersaturated drug separates into a drug-rich liquid or glassy phase; the highest free concentration reachable without crystals.
  • LLPS: liquid–liquid phase separation, here into a water-rich bulk phase and colloidal drug-rich droplets.
  • Free (bulk) concentration: drug molecularly dissolved in the water phase, measured in the supernatant after the droplets are spun down; it sets thermodynamic activity and so membrane flux.
  • Mole fraction (x1): the share of ritonavir molecules among the drug molecules in the drug-rich phase (water ignored).
  • Colligative effect: an effect that depends on the number of dissolved molecules, not their identity.
  • Pyrene I3/I1: the ratio of two pyrene emission peaks, which rises as its surroundings become less polar.
Fig. 1: Structures of the five drugs and HPMC
Fig. 1 · p.2585 · Structures of the five drugs and HPMCShows. ritonavir and lopinavir are structurally similar; diclofenac carries a carboxylic acid.

03Main findings

1

Each drug alone has a ceiling: its amorphous solubility

Ritonavir, lopinavir and paclitaxel formed a drug-rich phase at 26–28, 16–17.3 and 27.2–30.1 µg/mL by four methods, far above their crystal solubility (1.7, 2.7 and 0.32 µg/mL), and their flux stopped rising at the same concentrations. ···

Fig. 2: Flux versus concentration for ritonavir, lopinavir and paclitaxel
Fig. 2 · p.2586 · Flux versus concentration for ritonavir, lopinavir and paclitaxelShows. linear rise, then a plateau from the amorphous solubility.Also supports K1
More detail

The four estimates of the LLPS concentration agreed within error: ritonavir 28 (extinction), 26 (fluorescence), 26.2 (ultracentrifuge) and 27.3 µg/mL (flux break); lopinavir 17.3, 16, 17.1 and 16.1; paclitaxel 27.2, 28, 29 and 30.1. Felodipine values, taken from the literature, were 6 (extinction) and 5.1 µg/mL (flux), with a crystal solubility of 0.74 µg/mL. · Flux rose linearly with donor concentration and then levelled off: about 0.21–0.22 µg/min for ritonavir from 30 µg/mL, 0.13–0.14 for lopinavir from 20 µg/mL and 0.25–0.27 for paclitaxel from 30 µg/mL (read from Fig. 2). The break point was found by intersecting linear fits to the two regions. The authors read the linear part as thermodynamic activity rising with concentration and the plateau as constant activity once a drug-rich phase forms ("indicates"). · The paclitaxel crystal solubility is that of a hydrate. ·

Table 1: Crystal and amorphous solubility by four methods
Table 1 · p.2586 · Crystal and amorphous solubility by four methodsShows. the four LLPS estimates agree for each drug; crystal solubility far lower.
2

A second drug makes ritonavir separate at much lower concentration

With 10 µM lopinavir, paclitaxel or felodipine present, ritonavir formed a drug-rich phase at about 14, 10 and 12 µg/mL instead of about 26 µg/mL; at 20 µM paclitaxel it took only about 2 µg/mL. Ultracentrifugation of ritonavir–lopinavir mixtures showed both drugs depleted below either single-drug limit. ··

Fig. 4: LLPS onset of ritonavir with a second drug
Fig. 4 · p.2588 · LLPS onset of ritonavir with a second drugShows. (a) the pyrene ratio rises at much lower ritonavir with 10 µM partner; arrows mark single-drug limits. (b) Onset falls with partner concentration.Read it as. lower onset in (b) means the pair separates more readily.Also supports K2
More detail

Fluorescence. The onset of the pyrene I3/I1 rise (or of the felodipine emission at 430 nm) moved from about 26 µg/mL ritonavir alone to about 14 (10 µM lopinavir), 10 (10 µM paclitaxel) and 12 µg/mL (10 µM felodipine). · At 5, 10, 15 and 20 µM of the second drug, the ritonavir onset was about 22, 14, 10 and 6 µg/mL with lopinavir, 16, 10, 4 and 2 with paclitaxel, and 18, 12 and 4 (to 15 µM) with felodipine (read from Fig. 4b). Per mole, paclitaxel and felodipine lowered the onset more than lopinavir; the authors compared at equal molar concentration because they consider the effect "likely a colligative effect", and they write that ritonavir with paclitaxel or felodipine "appears" to separate most readily. · The second-drug concentration in these runs is given as 4 µg/mL in the methods and 10 µM in the results.

Ultracentrifugation. With 5 µg/mL ritonavir, all added lopinavir stayed in the supernatant up to 10 µg/mL; above about 15 µg/mL lopinavir levelled off at ≈15 µg/mL and ritonavir fell from ≈5 to ≈3.2 µg/mL. With 10 µg/mL ritonavir depletion began between 5 and 10 µg/mL lopinavir, with 15 µg/mL ritonavir by 5 µg/mL lopinavir, and with 30 µg/mL ritonavir (above its own limit) both drugs were depleted from the first addition (ritonavir ≈21 → ≈13 µg/mL as lopinavir rose from 5 to 30). All values were read from Fig. 3. Dissolved pellets matched the drug ratio expected by difference. The authors read this as one drug-rich phase containing both drugs ("consistent with"), forming at lower concentrations than for either drug alone. ··

Fig. 3: Both drugs depleted in ritonavir–lopinavir mixtures
Fig. 3 · p.2587 · Both drugs depleted in ritonavir–lopinavir mixturesShows. supernatant concentrations fall below the added amounts (dashed lines) at lower lopinavir as ritonavir rises from 5 to 30 µg/mL.
3

Lopinavir moves into an existing ritonavir-rich phase; ionized diclofenac does not

With a ritonavir drug-rich phase present (45 µg/mL ritonavir), only about a third of the lopinavir added stayed in solution, and about 0.21 of it at 85 µg/mL ritonavir (read from Fig. 6); bulk ritonavir fell as lopinavir was added. Diclofenac anion stayed fully in solution and ritonavir stayed at about 25 µg/mL. ··

Fig. 5: Lopinavir drawn into a ritonavir drug-rich phase
Fig. 5 · p.2588 · Lopinavir drawn into a ritonavir drug-rich phaseShows. a third of added lopinavir stays in bulk; bulk ritonavir falls.Also supports K3
Fig. 7: Diclofenac anion does not mix
Fig. 7 · p.2589 · Diclofenac anion does not mixShows. diclofenac recovered in full; ritonavir constant near 25 µg/mL.Also supports K3
More detail

Adding 4, 8, 12 and 16 µg/mL lopinavir to a 45 µg/mL ritonavir solution left ≈1.4, 2.8, 4.2 and 5.3 µg/mL lopinavir in bulk, a constant third, while bulk ritonavir fell from ≈23.6 to ≈19.8 µg/mL (read from Fig. 5). · With 16 µg/mL lopinavir, raising ritonavir to 65 and 85 µg/mL (more drug-rich phase) lowered bulk lopinavir from ≈5.3 to ≈4.15 and ≈3.4 µg/mL, about 0.33 to 0.21 of the added amount, while bulk ritonavir rose from ≈19.8 to ≈23.0 µg/mL; the text calls this "from about 1/3 to 1/4" and says it "confirms" that more drug-rich phase takes up more of a second lipophilic drug. ·· Diclofenac at 4–20 µg/mL was recovered in full (≈4.5–20.2 µg/mL) and ritonavir stayed at ≈25.1–25.7 µg/mL. · The authors explain the partitioning as preferential mixing of lopinavir into the ritonavir-rich phase, which in turn lowers ritonavir's own amorphous solubility (Fig. 10), and the absence of diclofenac mixing by its ionic charge ("readily explained"). · DLS gave a drug-rich phase of about 360 nm for 30 µg/mL ritonavir, 370 nm with 5 µg/mL lopinavir added and about 225 nm at 15 µg/mL ritonavir with 9 µg/mL lopinavir. ·

Fig. 6: More ritonavir-rich phase takes more lopinavir
Fig. 6 · p.2589 · More ritonavir-rich phase takes more lopinavirShows. bulk lopinavir falls as ritonavir rises from 45 to 85 µg/mL; bulk ritonavir rises.
4

In mixtures the free concentration and flux of both drugs fall

At 30 µg/mL of each drug, flux gave free ritonavir of 9.3 µg/mL with paclitaxel and 13.2 with lopinavir, and free paclitaxel and lopinavir of 14.8 and 8.5 µg/mL; ultracentrifugation gave the same values within error (8.2, 13.3, 15 and 9.1). ·

Table 2: Free concentration in 30 + 30 µg/mL mixtures
Table 2 · p.2590 · Free concentration in 30 + 30 µg/mL mixturesShows. flux and ultracentrifugation give the same reduced free concentrations.Also supports K4
More detail

In the diffusion cell each drug reached the receiver more slowly from a binary donor than from its single-drug donor at the same 30 µg/mL (Fig. 8): at 75 min about 0.24–0.26 versus 0.48 µg/mL for ritonavir, 0.33 versus 0.49 for paclitaxel, 0.21 versus 0.41 for lopinavir (read from Fig. 8). · Table 2 converts the binary fluxes into free concentrations with the single-drug flux curves and compares them with ultracentrifuged solutions of the same composition (n = 3): ritonavir 9.3 and 8.2 µg/mL with paclitaxel, 13.2 and 13.3 with lopinavir; paclitaxel 14.8 and 15; lopinavir 8.5 and 9.1. · The authors summarise ritonavir as falling "to just a third" of the added amount with paclitaxel and "a little less than half" with lopinavir, and paclitaxel and lopinavir by "a factor of around two"; the first two are relative to the 30 µg/mL added, the factor of two for lopinavir holds against its own amorphous solubility. · A binary solution with both drugs below their LLPS concentrations diffused at the single-drug rates (data not shown), which the authors take to exclude interactions in the bulk solution. ·· The ritonavir curves of Figs. 8a and 8b are closer to each other than the Table 2 values suggest.

Fig. 8: Receiver concentration versus time, single and binary donors
Fig. 8 · p.2590 · Receiver concentration versus time, single and binary donorsShows. each drug crosses the membrane more slowly when the other is present.
5

Ideal mixing in the drug-rich phase predicts the bulk concentrations, roughly

Plotted against ritonavir mole fraction in the drug-rich phase (about 0.06–0.70), bulk ritonavir rose from ≈3 to ≈21 µg/mL and lopinavir fell from ≈15 to ≈5 µg/mL, close to the no-fit ideal-mixing lines Sa° × x; ritonavir ran about 2–4 µg/mL above its line. ··

Fig. 9: Bulk concentrations versus drug-rich phase composition, with the ideal-mixing lines
Fig. 9 · p.2591 · Bulk concentrations versus drug-rich phase composition, with the ideal-mixing linesShows. ritonavir rises and lopinavir falls with ritonavir mole fraction; lines are Eq. 4 without fitting.Also supports K5
More detail

The lines use only the single-drug amorphous solubilities (about 26 µg/mL for ritonavir and 17 µg/mL for lopinavir; which Table 1 column is not stated) and assume constant aqueous activity coefficients, no size effect of droplets of about 350 nm, the same water content in single and mixed drug-rich phases, and single-drug values as Sa°. ·· Thirty-four ritonavir and 32 lopinavir points span x ≈0.06–0.70 (read from Fig. 9). Most ritonavir points lie above the line (for example ≈19.1 at x ≈0.56 against ≈14.7), and lopinavir points lie below it at mid-range (≈7.9–8.7 against ≈9.1–10.8 at x ≈0.37–0.47). The authors call the agreement "good" and conclude that ritonavir and lopinavir are miscible as amorphous materials in water and mix "nearly ideally"; a melting point depression of crystalline ritonavir by lopinavir larger than the Schröder–van Laar prediction (data not shown) is offered as confirmation. ·· An extractor check, not made in the paper, with the Table 2 ultracentrifuge values (30 + 30 µg/mL) gives x(ritonavir) ≈0.41 and predicted bulk concentrations of ≈10.8 (ritonavir) and ≈10.1 µg/mL (lopinavir) against 13.3 and 9.1 measured, the same pattern.

04Further observations

  • Paclitaxel crystallized without HPMC; ritonavir and lopinavir separated at the same concentration with or without it.
  • Drug-rich droplets measured about 225–370 nm by DLS.
  • Dissolved pellets matched the mass balance from the supernatants.
  • A binary solution below the LLPS concentrations diffused normally (data not shown).
More detail
  • HPMC matters for paclitaxel only. Without 10 µg/mL HPMC, paclitaxel crystallized during the ultracentrifuge measurement; ritonavir and lopinavir gave unchanged LLPS concentrations, so the reported values refer to solutions with a small amount of polymer. Whether HPMC was present in the fluorescence, extinction and binary experiments is not stated. ··
  • Droplet size. DLS gave about 360 nm for 30 µg/mL ritonavir, a similar 370 nm after adding 5 µg/mL lopinavir and about 225 nm at 15 µg/mL ritonavir with 9 µg/mL lopinavir (each slightly above half of its own LLPS concentration). The authors use the ≈350 nm size to argue that droplets are too large to raise solubility. ··
  • Mass balance. Pellets from some binary runs, dried and dissolved in methanol, matched the drug ratio obtained by subtracting the supernatant from the amount added.
  • No bulk-solution interaction. Ritonavir–lopinavir solutions below the LLPS concentration diffused at the single-drug rates (data not shown). The methods describe this control as 30 µg/mL ritonavir with 12 µg/mL lopinavir, where Fig. 3 already shows phase separation at 30 + 10 µg/mL. ··
  • Pyrene response. The I3/I1 ratio was about 0.51 without and about 0.61 with a drug-rich phase (methods); the baselines in Fig. 4a sit near 0.53. ·

05How the authors connect the findings

1Below its amorphous solubility a drug's activity, and so its flux, rises with concentration; above it a drug-rich phase forms and the activity is fixed. ·
↓
2Amorphous drugs are liquid-like and can mix, so with two unionized drugs present the drug-rich phase contains both. ·
↓
3In an ideal mixture each drug's chemical potential in the drug-rich phase drops by RT ln x, so its amorphous solubility drops to Sa° × x. ··
↓
Miscible unionized partnerIt joins the drug-rich phase↓each drug's mole fraction falls below 1↓lower amorphous solubility of each↓earlier LLPS, lower free concentration and lower flux.··
Ionized partnerIts charge keeps it out of the hydrophobic drug-rich phase↓no mixing↓its own and ritonavir's free concentrations unchanged.·
What sets the size of the drop. Each drug's mole fraction in the shared drug-rich phase: the more drug-rich phase of one drug, the more of the other it takes up; non-ideal pairs "are likely" to behave differently. ··
Conclusion drawn. Two highly supersaturated drugs lower each other's thermodynamic activity ("clearly demonstrated"), so co-formulated amorphous drugs "would be expected" to reach lower supersaturation. ·
Fig. 10: Lopinavir mixing into the ritonavir drug-rich phase (schematic)
Fig. 10 · p.2592 · Lopinavir mixing into the ritonavir drug-rich phase (schematic)Shows. added lopinavir (red) enters ritonavir droplets; more ritonavir raises its mole fraction in them.
More detail
  1. Single-drug flux rises linearly up to the amorphous solubility and then stays flat, because the drug-rich phase fixes the chemical potential of the dissolved drug ("indicates"). ··
  2. Amorphous drugs have a liquid-like structure and can mix with other compounds. When a second unionized lipophilic drug is present, it distributes between water and the drug-rich phase according to its affinity for each and their amounts ("It is anticipated"); the depletion of both drugs in ultracentrifuged mixtures is read as one mixed drug-rich phase. ··
  3. With ideal mixing, Eq. 2 and Eq. 3 lower each drug's chemical potential by RT ln of its mole fraction, and Eq. 4 follows: the free concentration in equilibrium with the mixed phase is Sa° × x. The drop in maximum flux in mixtures "suggests" that each drug's amorphous solubility is lowered by the other, which conventional thermodynamics explains. ···
  4. The onset of LLPS moves to lower concentrations than for either drug alone; the authors call this "likely a colligative effect" and therefore compare partners at equal molar concentration. ·

[-] Miscible unionized partner (lopinavir, paclitaxel, felodipine). The partner enters the drug-rich phase → ritonavir's mole fraction falls → its amorphous solubility falls, and so does the partner's → lower free concentrations of both and lower flux across the membrane. Adding a small amount of lopinavir to an existing ritonavir-rich phase pulls most of it into that phase and lowers bulk ritonavir too (Fig. 10). ··

[+] Ionized partner (diclofenac anion). The charge makes mixing with the hydrophobic ritonavir-rich phase energetically unfavourable ("readily explained") → no mixing → unchanged free concentrations. ·

What sets the size of the drop. The mole fraction of each drug in the drug-rich phase: the reduction is "highly dependent" on it. More drug-rich phase of one drug takes up a larger share of the other. Lopinavir and ritonavir mix "fairly ideally", perhaps from structural similarity; other pairs "are likely" to be non-ideal, up to immiscibility. ··

Conclusion drawn. The thermodynamic activity of a highly supersaturated drug is "considerably reduced" by a second solute, especially one that is also highly supersaturated; co-formulating amorphous drugs "would be expected" to lower achievable supersaturation and membrane transport. ·

06What it means for formulation

Stated by the authors
  • Co-formulating two amorphous drugs would lower each drug's amorphous solubility, achievable supersaturation and membrane transport.
  • This deserves attention for HIV and hepatitis C antivirals, often formulated or dosed together.
  • In metabolic assays a drug-rich phase can deplete neutral substrates and cause false positives.
AI reading, not stated in the paper
  • In a two-drug supersaturating product, each drug's ceiling is its own amorphous solubility times its mole fraction in the shared phase; the minor drug loses most.
More detail
Stated by the authors
  • Co-formulation of two or more amorphous drugs "would be expected" to reduce the amorphous solubility of each, giving lower achievable supersaturation and lower membrane transport; a similar effect was reported for a ritonavir–darunavir ASD. ··
  • The reduced supersaturation has "potential implications" for bioavailability, precipitation and conversion to crystals; it is "of particular relevance" to HIV and hepatitis C antivirals, which are very poorly soluble and often formulated or dosed with other compounds.
  • The results apply to fixed-dose combinations and to drugs dosed together that supersaturate in the gut (ASDs, weak bases and salts, lipid formulations), and should be considered when developing co-amorphous or other supersaturating formulations. ·
  • In in vitro metabolic assays, aggregates of a neutral test compound would lower the free concentration of miscible unionized substrates, "potentially" causing false positives for inhibition; ionized substrates such as diclofenac would not be affected.
  • Drug in nanosized droplets "may" absorb UV and inflate the apparent dissolved concentration, and turbidity from droplets "may be mistaken" for crystallization.
AI reading, not stated in the paper
  • For two drugs that both supersaturate, the free-concentration ceiling of each is roughly Sa° × x, where x is its mole fraction in the shared drug-rich phase. The drug present in the smaller molar amount loses most, so dose ratio matters as much as drug choice.
  • A boosting drug dosed above its own amorphous solubility, such as ritonavir, may act as a sink for a co-dosed lipophilic drug; ionization of the partner at gut pH would protect it.
  • Whether two drugs mix in the amorphous state (for example, by melting point depression or a co-amorphous screen) is a cheap first check of this risk.
  • The drug-rich phase may still act as a reservoir that replenishes free drug; this paper measured only free concentration and flux across a dialysis membrane, not absorption.

07Open questions

Raised by the authors
  • How do non-ideal pairs behave, up to immiscibility?
  • What do lower amorphous solubilities mean for bioavailability and crystallization of co-formulated drugs?
Not covered by this paper (AI reading)
  • No co-amorphous or two-drug ASD was dissolved; all solutions came from methanol stocks.
  • The model was tested on one pair, and ritonavir ran above it.
More detail
Raised by the authors
  • Other drug pairs are "likely" to mix less ideally, down to immiscibility; this was shown only for an ionized partner. ·
  • Reduced achievable supersaturation has "potential implications" for bioavailability, precipitation and crystallization that remain to be studied.
Not covered by this paper (AI reading)
  • No formulation was tested: all solutions were made by adding methanolic stocks to buffer, so dissolution of co-amorphous or two-drug ASD products was not studied.
  • The ideal-mixing model was tested only for ritonavir–lopinavir, and ritonavir sits systematically above it; mixed drug-rich phase compositions for paclitaxel and felodipine were not measured.
  • The colligative explanation was not tested, for example by comparing solutes at equal molar concentration and different structure in the ultracentrifuge.
  • Equilibration time, HPMC presence and crystallization over time in the binary experiments were not reported.
  • Only one buffer, no bile salts or biorelevant media, and one temperature (25 °C where stated).

08How solid

AI assessment, not a statement made in the paper
Strong

The central result, that a second miscible drug lowers each drug's free concentration and flux, rests on three methods that agree (fluorescence onset, ultracentrifugation, flux), with flux and ultracentrifugation matching within error at n = 3. ·· The ideal-mixing model and the formulation implications are weaker: the model fits one pair, roughly, and no formulation was tested. ·

More detail
What holds
  • Single-drug amorphous solubilities agree across four independent methods.
  • Free concentrations in mixtures from flux and from ultracentrifugation agree within error (n = 3).
  • The lowered LLPS onset is seen by fluorescence for three partners and by ultracentrifugation for lopinavir, with a consistent dependence on partner concentration. ··
  • The partition of lopinavir into a ritonavir drug-rich phase is consistent across Figs. 5 and 6, with an ionized negative control. ··
What weakens it
  • Ritonavir points lie systematically above the ideal-mixing line; agreement is not quantified; only one pair was modelled. ·
  • Most data are plot readings with replicates not stated; Fig. 8 does not match Table 2 well for the paclitaxel system.
  • The below-LLPS control is described inconsistently and its data are not shown.
  • The concentration of the second drug in the fluorescence runs is given as 4 µg/mL and as 10 µM.
  • The reductions are stated against different baselines, and paclitaxel at 30 µg/mL is at, not below, its LLPS concentration. ·
  • HPMC presence and equilibration time in the binary experiments are not stated.
  • The formulation, assay and bioavailability implications are not tested. ··

09Figure guide

Every figure and table of the paper, what it is there for, and what to check on the original. Key figures are shown with the story.

FigureWhat it does in the paperSupportsCheck (AI note)
Fig. 1 (p.2585)key figureDefines the systems: structures of ritonavir, lopinavir, paclitaxel, felodipine, diclofenac and HPMC.·····0.2
Table 1 (p.2586)key figurePins each drug's amorphous solubility by four methods against its crystal solubility.F1Felodipine values cited to ref 16; source unclear.
Fig. 2 (p.2586)key figureShows flux rising linearly and then flat from the amorphous solubility for three drugs.F1, K1
Fig. 3 (p.2587)key figureShows both drugs depleted from the supernatant in ritonavir–lopinavir mixtures, earlier at higher ritonavir.F2No error bars; n not stated.
Fig. 4 (p.2588)key figureShows the ritonavir LLPS onset lowered by lopinavir, paclitaxel and felodipine, and its dependence on partner concentration.·F2, K2Partner given as 4 µg/mL in methods, 10 µM in results; baseline ratio ≈0.53, not 0.51.·
Fig. 5 (p.2588)key figureShows a third of added lopinavir staying in bulk with a ritonavir drug-rich phase present.F3, K3
Fig. 6 (p.2589)key figureShows more ritonavir-rich phase pulling more lopinavir out of solution.F3Plot gives ≈0.21 of added, text "1/4".
Fig. 7 (p.2589)key figureIonized control: diclofenac fully recovered, ritonavir unchanged.F3, K3
Fig. 8 (p.2590)key figureShows slower membrane transport of each drug from binary donors.F4Text swaps panels a and b; ritonavir curves closer than Table 2.·
Table 2 (p.2590)key figureGives the reduced free concentrations from flux and ultracentrifugation.F4, K4Reductions stated against different baselines.
Fig. 9 (p.2591)key figureTests the ideal-mixing model against ritonavir–lopinavir bulk data.F5, K5Ritonavir points above the line; Sa° column not stated.·
Fig. 10 (p.2592)key figureSchematic of lopinavir mixing into the ritonavir drug-rich phase.0.5A schematic, not data.